13F

Investor

RA CAPITAL MANAGEMENT, L.P.

CIK 0001346824 · filed 2026-05-15 · SEC filing

13F book

$9.44B

Positions

85

24 new · 10 sold

Largest name

24.9%

Ascendis Pharma A/S · ASND

Est. mark

$3.2M

Price effect on 61 names still held. Flow −$326.3M.
NameTickerSharesValueWeightEst. markChange
Ascendis Pharma A/SASND10.3M$2.35B24.9%$159.3MHeld
Vaxcyte, Inc.PCVX11.5M$666.8M7.1%$128.4MAdded$172M
Rhythm Pharmaceuticals, Inc.RYTM6.67M$579.8M6.1%−$133.8MHeld
Tyra Biosciences, Inc.TYRA12.2M$467.2M5.0%$146.5MHeld
Sionna Therapeutics, Inc.SION9.91M$397.1M4.2%−$10.4MHeld
Edgewise Therapeutics, Inc.EWTX10.4M$328.5M3.5%$69.7MHeld
Newamsterdam Pharma Company9.55M$305.7M3.2%−$29.3MHeld
Nuvalent Inc2.53M$259.6M2.8%$3.5MAdded$70.5M
Dianthus Therapeutics Inc2.61M$219.2M2.3%$68.8MAdded$152.8M
Mineralys Therapeutics, Inc.MLYS7.69M$208.4M2.2%−$67.4MAdded−$57.4M
SpyGlass Pharma, Inc.SGP8.02M$207.8M2.2%New
Wave Life Sciences Ltd.WVE27M$195.6M2.1%−$177.5MAdded−$113.9M
Septerna, Inc.SEPN7M$168.1M1.8%−$26.9MHeld
Disc Medicine, Inc.IRON2.45M$156.7M1.7%−$30.6MAdded−$257.5K
Janux Therapeutics, Inc.JANX11.2M$155.5M1.6%$1.12MHeld
Biocryst Pharmaceuticals IncBCRX15.8M$150.7M1.6%$27.2MHeld
Bicara Therapeutics Inc.BCAX7.26M$144.3M1.5%$21.3MAdded$27.3M
Praxis Precision Medicines I373.8K$120.4M1.3%$10.3MHeld
Gh Research PlcGHRS7.68M$107.9M1.1%$10.4MHeld
Zai Lab LtdZLAB5.71M$107.4M1.1%New
Taysha Gene Therapies, Inc.TSHA23.6M$105.3M1.1%−$24.3MHeld
Vor Biopharma Inc.VOR5.4M$96.4M1.0%$25.7MHeld
Geron CorpGERN63.8M$95M1.0%$10.8MHeld
ARS Pharmaceuticals, Inc.SPRY10.9M$87.2M0.9%−$39.3MHeld
Sarepta Therapeutics, Inc.SRPT3.9M$84.9M0.9%New
Spyre Therapeutics, Inc.SYRE1.62M$81.8M0.9%$28.7MHeld
Evommune, Inc.EVMN3.49M$80.3M0.9%$20.3MAdded$21.1M
Climb Bio, Inc.CLYM11.3M$77.4M0.8%−$348.5KAdded−$299.8K
Solid Biosciences Inc.SLDB9.34M$67.2M0.7%$9.07MAdded$34.5M
Artiva Biotherapeutics, Inc.ARTV9.85M$63.5M0.7%$21.2MHeld
Galecto IncDMRA2.4M$62.1M0.7%New
Xencor IncXNCR4.9M$59.1M0.6%New
Lb Pharmaceuticals IncLBRX2.21M$54.5M0.6%$5.3MHeld
Jade Biosciences, Inc.JBIO3.67M$51.6M0.5%−$5.07MHeld
Acumen Pharmaceuticals, Inc.ABOS21M$49.5M0.5%$3.73MAdded$18M
4d Molecular Therapeutics In5.05M$47M0.5%$9.14MCut$4.61M
Fulcrum Therapeutics, Inc.FULC6.05M$46.4M0.5%−$22MHeld
Capricor Therapeutics, Inc.CAPR1.51M$45.8M0.5%$2.32MHeld
Century Therapeutics, Inc.IPSC17.8M$40.1M0.4%New
Olema Pharmaceuticals, Inc.OLMA2.6M$38.8M0.4%−$26.2MHeld
LENZ Therapeutics, Inc.LENZ4.18M$38.2M0.4%−$28.6MHeld
Monopar TherapeuticsMNPR667.2K$36.6M0.4%−$7.01MHeld
PepGen Inc.PEPG20.1M$35.5M0.4%−$95.1MHeld
Design Therapeutics, Inc.DSGN2.97M$31.6M0.3%$1.84MAdded$17.9M
Mirum Pharmaceuticals, Inc.MIRM318.6K$29.4M0.3%New
BioAge Labs, Inc.BIOA1.65M$28.9M0.3%New
Lexeo Therapeutics, Inc.LXEO5M$28.7M0.3%−$20.9MHeld
Assembly Biosciences, Inc.ASMB1.02M$28.3M0.3%−$6.39MHeld
Rezolute, Inc.RZLT9.18M$28M0.3%$6.33MHeld
Aktis Oncology, Inc.AKTS1.5M$26.9M0.3%New
Alx Oncology Hldgs Inc13M$26.1M0.3%New
Aclaris Therapeutics, Inc.ACRS6.8M$25.5M0.3%New
Ovid Therapeutics Inc.OVID10.7M$23.8M0.3%$6.32MHeld
Nkarta, Inc.NKTX10.8M$22.8M0.2%$2.81MHeld
Travere Therapeutics, Inc.TVTX746.8K$22.2M0.2%New
GRAIL, Inc.GRAL428.3K$22.1M0.2%−$14.5MHeld
C4 Therapeutics, Inc.CCCC8M$21M0.2%$5.76MHeld
Relmada Therapeutics, Inc.RLMD2.95M$20.5M0.2%New
Benitec Biopharma Inc.BNTC1.85M$19.7M0.2%−$5.22MHeld
Bright Minds Biosciences Inc.DRUG265K$19.3M0.2%New
Sutro Biopharma, Inc.STRO715.3K$17.8M0.2%New
Contineum Therapeutics, Inc.CTNM1.3M$16.9M0.2%$2.11MCut−$7.99M
Sab Biotherapeutics Inc4.4M$16.9M0.2%$396.1KHeld
Inspire Med Sys Inc325.7K$16.8M0.2%−$5.77MAdded$3.7M
Anteris Technologies Global Corp.AVR3M$16.6M0.2%New
OnKure Therapeutics, Inc.OKUR4M$16.6M0.2%New
Hinge Health, Inc.HNGE364.6K$14.1M0.1%−$632.1KAdded$10.3M
GeneDx Holdings Corp.WGS209.9K$13.5M0.1%−$3.82MAdded$5.93M
Waystar Hldg Corp529.4K$12.8M0.1%−$1.25MAdded$8.03M
Helix Acquisition Corp. IIIHLXC1.25M$12.7M0.1%New
Palisade Bio, Inc.PALI7.12M$12.5M0.1%−$4.27MHeld
Acrivon Therapeutics, Inc.ACRV8.34M$11.6M0.1%−$8.51MHeld
Atrium Therapeutics, Inc.RNA864.1K$11.6M0.1%New
Karyopharm Therapeutics Inc.KPTI1.92M$10.7M0.1%New
Avalo Therapeutics, Inc.AVTX663K$9.9M0.1%−$2.14MHeld
Perceptive Cap Solutions Cor750K$8.23M0.1%−$1.54MHeld
Adicet Bio, Inc.ACET1.18M$8.05M0.1%−$1.53MAdded$69.4K
Newamsterdam Pharma Company333.3K$6.68M0.1%−$986.7KHeld
Corvus Pharmaceuticals, Inc.CRVS450K$6.58M0.1%New
Rani Therapeutics Hldgs Inc8.5M$6.25M0.1%−$5.23MHeld
Equillium, Inc.EQ3.1M$6.19M0.1%New
Werewolf Therapeutics, Inc.HOWL6.68M$5.56M0.1%$1.33MHeld
Macrogenics IncMGNX1.86M$5.39M0.1%New
MapLight Therapeutics, Inc.MPLT248.3K$5.05M0.1%New
Palatin Technologies IncPTN70K$1.22M0.0%$142.8KHeld

Positions as of Q1 2026. 13F filings arrive up to 45 days after quarter-end and omit shorts. Values are quarter-end marks, as filed. Estimated mark is the price effect on shares still held — not realized P&L or investment advice.